For the committee, some of the reasons it used to reject adding Pompe disease to Australia’s newborn bloodspot screening programs are perversely the same as those it invoked to support the addition of Hurler (MPS I) and Hunter (MPS II) syndromes.
Decision-making at its nadir, exposing the cruelty of incoherence
September 16, 2025 Latest NewsBioPharmaComment
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